“On Saturday, researchers reported the first data indicating that the experimental treatment worked, causing levels of the destructive protein to plummet in Doherty’s body and the bodies of five other patients treated with the approach.”
This is the first time CRISPR has been injected into the bloodstream to edit genes inside the body, not in a dish. Six patients is a tiny trial, and the company sponsoring it is the one doing the talking. The early numbers are still real. If the effect lasts, a lot of drugs that people take for life become a single infusion.